Is a
Patent attributes
Patent Jurisdiction
Patent Number
Date of Patent
September 20, 2022
0Patent Application Number
173656140
Date Filed
July 1, 2021
0Patent Primary Examiner
Provided herein are nucleic acids, recombinant adeno-associated viral particles, compositions and methods related to treating Friedreich's ataxia. In some examples, the nucleic acids, recombinant adeno-associated viral particles, compositions and methods involve us of a FXN coding sequence, a truncated FXN 3′ UTR, and a prompter.
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