Is a
Patent attributes
Patent Applicant
Current Assignee
Patent Jurisdiction
Patent Number
Patent Inventor Names
Frank Rigo0
Katherine M. Bishop0
Date of Patent
October 8, 2019
Patent Application Number
15509642
Date Filed
September 11, 2015
Patent Citations Received
Patent Primary Examiner
Patent abstract
Disclosed herein are compounds, compositions and methods for modulating splicing of SMN2 mRNA in a subject. Also provided are uses of disclosed compounds and compositions in the manufacture of a medicament for treatment of diseases and disorders, including spinal muscular atrophy. Also provided are kits for detecting the amount of SMN protein in a sample of cerebrospinal fluid.
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