Is a
Patent attributes
Patent Jurisdiction
Patent Number
Patent Inventor Names
Steven Gray0
Date of Patent
November 22, 2022
0Patent Application Number
163053370
Date Filed
June 13, 2017
0Patent Citations
Patent Primary Examiner
CPC Code
This invention relates to polynucleotides comprising a nucleotide sequence encoding a PPT1 polypeptide or a fragment thereof, vectors (viral or non-viral vectors) comprising the same, and methods of using the same for delivery of the open reading frame to a cell or a subject and to treat infantile neuronal lipofuscinosis (infantile Batten disease). The polynucleotides comprise an optimized CLN1 open reading frame.
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