Patent 9434928 was granted and assigned to Nationwide Children's Hospital on September, 2016 by the United States Patent and Trademark Office.
The present invention relates to recombinant adeno-associated virus (rAAV) delivery of an alpha-sarcoglycan gene. The invention provides rAAV products and methods of using the rAAV in the treatment of limb girdle muscular dystrophies such as LGMD2D.