Is a
Patent attributes
Patent Jurisdiction
Patent Number
Date of Patent
October 25, 2022
Patent Application Number
16864911
Date Filed
May 1, 2020
Patent Citations
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Patent Primary Examiner
Aspects of the disclosure relate to a gene therapy approach for diseases, disorders, or conditions caused by mutation in the stop codon utilizing modified tRNA. At least 10-15% of all genetic diseases, including muscular dystrophy (e.g. Duchene muscular dystrophy), some cancers, beta thalassemia, Hurler syndrome, and cystic fibrosis, fall into this category. Not to be bound by theory, it is believed that this approach is safer than CRISPR approaches due to minimal off-target effects and the lack of genome level changes.
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