Is a
Patent attributes
Patent Applicant
Current Assignee
Patent Jurisdiction
Patent Number
Patent Inventor Names
Christian Mueller0
Phillip D. Zamore0
Terence Flotte0
Date of Patent
February 6, 2018
Patent Application Number
14952217
Date Filed
November 25, 2015
Patent Citations Received
Patent Primary Examiner
Patent abstract
The invention relates to isolated nucleic acids and rAAV-based compositions, methods and kits useful for treating genetic diseases (e.g., alpha-1 antitrypsin deficiency).
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