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US Patent 12123002 Compositions and methods of treating amyotrophic lateral sclerosis (ALS)

Patent 12123002 was granted and assigned to Voyager Therapeutics on October, 2024 by the United States Patent and Trademark Office.

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 US Patent 12123002 Compositions and methods of treating amyotrophic lateral sclerosis (ALS)

Article

Patent abstract

The present invention relates to small interfering RNA (siRNA) molecules against the SOD1 gene, adeno-associated viral (AAV) vectors encoding siRNA molecules and methods for treating amyotrophic lateral sclerosis (ALS) using the siRNA molecules and AAV vectors.

Infobox
Is a
Patent
Patent
0
Patent Applicant
Voyager Therapeutics
Voyager Therapeutics
0
Current Assignee
Voyager Therapeutics
Voyager Therapeutics
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Patent Jurisdiction
United States Patent and Trademark Office
United States Patent and Trademark Office
0
Patent Number
121230020
Patent Inventor Names
Dinah Wen-Yee Sah0
Jinzhao Hou0
Jochen Deckert0
Markus Hossbach0
Mathieu E. Nonnenmacher0
Pengcheng Zhou0
Date of Patent
October 22, 2024
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Patent Application Number
180852220
Date Filed
December 20, 2022
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Patent Citations
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Patent Primary Examiner
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Ekaterina Poliakova-Georgantas
0

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